Three persons treated w gene therapy for LCA showed visual acuity improved, then declined.

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$uniQure(QURE)$  $Celladon Corporation(CLDN)$  $Avalanche Biotechnologies(AAVL)$  $BLUEBIRD BIO INC(BLUE)$  $Applied Genetic Technologies(AGTC)$  $SPARK THERAPEUTICS INC(ONCE)$